Detalhe da pesquisa
1.
Gene Therapy in Patients with Transfusion-Dependent ß-Thalassemia.
N Engl J Med
; 378(16): 1479-1493, 2018 04 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-29669226
2.
Gene Therapy in a Patient with Sickle Cell Disease.
N Engl J Med
; 376(9): 848-855, 2017 03 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-28249145
3.
New dosing nomogram and population pharmacokinetic model for young and very young children receiving busulfan for hematopoietic stem cell transplantation conditioning.
Pediatr Blood Cancer
; 67(10): e28603, 2020 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-32706505
4.
Haploidentical Hematopoietic Stem Cell Transplantation with Post-Transplant Cyclophosphamide for Primary Immunodeficiencies and Inherited Disorders in Children.
Biol Blood Marrow Transplant
; 25(7): 1363-1373, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30876929
5.
Midostaurin in Advanced Systemic Mastocytosis.
N Engl J Med
; 374(26): 2605-7, 2016 Jun 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-27355555
6.
Long-term outcomes of lentiviral gene therapy for the ß-hemoglobinopathies: the HGB-205 trial.
Nat Med
; 28(1): 81-88, 2022 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-35075288
7.
Intensive chemotherapy followed by autologous stem cell transplantation in primary central nervous system lymphomas (PCNSLs). Therapeutic outcomes in real life-experience of the French Network.
Bone Marrow Transplant
; 57(6): 966-974, 2022 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-35422077
8.
New ifosfamide analogs designed for lower associated neurotoxicity and nephrotoxicity with modified alkylating kinetics leading to enhanced in vitro anticancer activity.
J Pharmacol Exp Ther
; 328(2): 598-609, 2009 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-19017849
9.
Unravelling the pharmacologic opportunities and future directions for targeted therapies in gastro-intestinal cancers Part 1: GI carcinomas.
Pharmacol Ther
; 174: 145-172, 2017 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-28223233
10.
Intracerebral gene therapy in children with mucopolysaccharidosis type IIIB syndrome: an uncontrolled phase 1/2 clinical trial.
Lancet Neurol
; 16(9): 712-720, 2017 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-28713035
11.
Microbiological and physicochemical stability of fentanyl and sufentanil solutions for patient-controlled delivery systems.
J Pain Symptom Manage
; 32(1): 90-7, 2006 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-16824989
12.
Application of an acceptance sampling plan for post-production quality control of chemotherapeutic batches in an hospital pharmacy.
Eur J Pharm Biopharm
; 64(1): 92-8, 2006 Aug.
Artigo
em Inglês
| MEDLINE | ID: mdl-16750352
13.
Gene Therapy of the ß-Hemoglobinopathies by Lentiviral Transfer of the ß(A(T87Q))-Globin Gene.
Hum Gene Ther
; 27(2): 148-65, 2016 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-26886832
14.
Plasma and intraprostatic concentrations of ertapenem following preoperative single dose administration: a single-centre prospective experience and clinical implications-the ERTAPRO study.
Int J Antimicrob Agents
; 48(2): 168-74, 2016 Aug.
Artigo
em Inglês
| MEDLINE | ID: mdl-27324263
15.
In vitro echogenicity characterization of poly[lactide-coglycolide] (plga) microparticles and preliminary in vivo ultrasound enhancement study for ultrasound contrast agent application.
Invest Radiol
; 40(8): 536-44, 2005 Aug.
Artigo
em Inglês
| MEDLINE | ID: mdl-16024992
16.
Liquid chromatography-mass spectrometry assay for quantitation of ifosfamide and its N-deschloroethylated metabolites in rat microsomal medium.
J Chromatogr B Analyt Technol Biomed Life Sci
; 820(2): 251-9, 2005 Jun 25.
Artigo
em Inglês
| MEDLINE | ID: mdl-15899378
17.
Fluorescence detection combined with either HPLC or HPTLC for pharmaceutical quality control in a hospital chemotherapy production unit: application to camptothecin derivatives.
J Pharm Biomed Anal
; 39(3-4): 581-6, 2005 Sep 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-16023817
18.
Quality control and stability study using HPTLC: applications to cyclophosphamide in various pharmaceutical products.
J Pharm Biomed Anal
; 38(1): 180-5, 2005 Jun 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-15907638
19.
Physicochemical and microbiological stability of azathioprine in InOrpha suspending agent studied under various conditions.
Int J Pharm Compd
; 19(1): 73-7, 2015.
Artigo
em Inglês
| MEDLINE | ID: mdl-25902631
20.
State of the art and future directions of pancreatic ductal adenocarcinoma therapy.
Pharmacol Ther
; 155: 80-104, 2015 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-26299994